Welcome to the Clinical Study for Wiskott-Aldrich Syndrome
What is Wiskott-Aldrich Syndrome (WAS)?
Wiskott-Aldrich Syndrome is an inherited disease of the immune system that may lead to frequent infections, bleeding and eczema (a skin rash). Currently there is no perfect treatment for patients with WAS.
What causes WAS?
WAS is a result of a gene mutation that affects the body's ability to make certain types of white blood cells that help the immune system fight infection. In WAS, there are too few white blood cells called lymphocytes. Some of the lymphocytes called natural killer cells are present in normal numbers but do not function properly. The natural killer cells do not work well and result in cancer and infections because WAS patients do not make enough IL-2. IL-2 is a type of natural protein produced by the body called a cytokine.
About this study...
We are doing this study to see if IL-2 research therapy can improve the way the immune system works in WAS. We want to improve the way the immune system works in individuals with WAS because currently there is no perfect treatment for this condition. If you are interested in this study and would like more information please contact us.